July 29, 2020
Thrive Earlier Detection
Thrive Earlier Detection Closes $257 Million Series B Financing
July 29, 2020
Editas Medicine
Catalent Enters Into Strategic Partnership With Editas Medicine To Support Gene Editing Medicine Pipeline
July 29, 2020
bluebird bio
Bristol Myers Squibb and bluebird bio Announce Submission of Biologics License Application (BLA) to FDA for Idecabtagene Vicleucel (Ide-cel, bb2121) for Adults with Relapsed and Refractory Multiple Myeloma
July 27, 2020
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals Announces Appointment of Joseph Shulman as Senior Vice President of Technical Operations
July 27, 2020
Editas Medicine
Editas Medicine Appoints Gad Berdugo As Chief Business Officer
July 27, 2020
Allena Pharmaceuticals
Allena Pharmaceuticals Announces $5.0 Million Bought Deal Offering
July 27, 2020
Allena Pharmaceuticals
Allena Pharmaceuticals Increases Previously Announced Bought Deal to $6.7 Million
July 24, 2020
Blueprint Medicines
Blueprint Medicines Receives Positive CHMP Opinion for Avapritinib for the Treatment of Adults with Unresectable or Metastatic PDGFRA D842V Mutant Gastrointestinal Stromal Tumors
July 23, 2020
Blueprint Medicines
Blueprint Medicines to Report Second Quarter 2020 Financial Results on Thursday, July 30, 2020
July 23, 2020
Editas Medicine
Editas Medicine To Host Conference Call Discussing Second Quarter 2020 Results And Corporate Update
July 23, 2020
MyoKardia
MyoKardia Announces Receipt of Breakthrough Therapy Designation from FDA for Mavacamten for the Treatment of Symptomatic, Obstructive Hypertrophic Cardiomyopathy
July 23, 2020
Nurix Therapeutics
Nurix Therapeutics Announces Pricing of $209 Million Initial Public Offering
July 21, 2020
MyoKardia
MyoKardia and Fulcrum Therapeutics Announce Multi-Target Collaboration to Discover Novel Targeted Therapies for Genetic Cardiomyopathies
July 21, 2020
Sage Therapeutics
Sage Therapeutics to Report Second Quarter 2020 Financial Results on Monday, August 10, 2020
July 20, 2020
Relay Therapeutics
Relay Therapeutics Announces Closing of Initial Public Offering and Full Exercise of Underwriters’ Option to Purchase Additional Shares
July 20, 2020
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals Announces Appointment of David Meeker, M.D., as Chief Executive Officer
July 16, 2020
Agios Pharmaceuticals
Agios to Webcast Conference Call of Second Quarter 2020 Financial Results on July 30, 2020
July 16, 2020
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals Announces Publication of Results from Phase 2 Study of Setmelanotide in Bardet-Biedl Syndrome in Diabetes, Obesity and Metabolismr
July 15, 2020
Relay Therapeutics
Relay Therapeutics Announces Pricing of Initial Public Offering
July 14, 2020
Blueprint Medicines
Blueprint Medicines Announces Global Collaboration with Roche to Develop and Commercialize Pralsetinib for Patients with RET-Altered Cancers
July 13, 2020
Nurix Therapeutics
Nurix Therapeutics Announces Addition of Dr. Jason Kantor to its Management Team
July 07, 2020
Editas Medicine
Editas Medicine And Azzur Group Announce A Multi-Year Agreement For EDIT-301 And EDIT-201 Manufacturing
July 06, 2020
MyoKardia
MyoKardia Announces Appointment of Denelle J. Waynick as General Counsel and Corporate Secretary
July 01, 2020
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals Receives Rare Pediatric Disease Designation from U.S. Food and Drug Administration for Setmelanotide for Treatment of POMC and LEPR Deficiency Obesities
July 01, 2020
Rhythm Pharmaceuticals
Rhythm Pharmaceuticals Announces Submission of Marketing Authorization Application to the European Medicines Agency for Setmelanotide in POMC and LEPR Deficiency Obesities
July 01, 2020
Celsius Therapeutics
Celsius Therapeutics Signs Research Agreements with Leading Academic Centers to Develop Insights into Inflammatory Bowel Disease Biology
July 01, 2020
Blueprint Medicines
Blueprint Medicines Announces Submission of New Drug Application to FDA for Pralsetinib for the Treatment of Advanced RET Mutant and RET Fusion-Positive Thyroid Cancers
June 30, 2020
Revolution Medicines
Revolution Medicines Reports New Application of Tri-Complex Modality for “Undruggable” Protein Targets and Announces License to Ginkgo Bioworks to Explore Potential Use Against Novel Coronavirus
June 30, 2020
Goldfinch Bio
Goldfinch Bio Secures $100 Million in Series B Financing
June 29, 2020
Blueprint Medicines
Blueprint Medicines Announces Publication in The Lancet Oncology Showing Durable Clinical Benefits of AYVAKIT™ (avapritinib) in NAVIGATOR Trial Patients with PDGFRA D842V Mutant GIST
June 25, 2020
Nurix Therapeutics
Nurix Therapeutics Announces Formation Of DeCART Therapeutics To Advance New CAR T Therapies Using Targeted Protein Modulation
June 25, 2020
GBT
GBT Awards $250,000 in ACCEL Grants to Advance Access to Care for People Living with Sickle Cell Disease
June 24, 2020
GBT
GBT Announces Plans to Seek Regulatory Approval for Oxbryta® (voxelotor) to Treat Sickle Cell Patients in Europe
June 24, 2020
Fulcrum Therapeutics
Fulcrum Therapeutics Announces Initiation of Multi-Center Phase 3 (LOSVID) Trial with Losmapimod for Hospitalized COVID-19 Patients
June 22, 2020
CytomX Therapeutics
CytomX Therapeutics Announces Preclinical Data from Anti-CTLA-4 Probody Therapeutic Programs Presented by Partner Bristol Myers Squibb at AACR Annual Meeting
June 22, 2020
Jounce Therapeutics
Jounce Therapeutics Presents First Preclinical Data on Anti-CCR8 Antibody JTX-1811 and Vopratelimab Translational Data at The American Association for Cancer Research Virtual Annual Meeting
June 19, 2020
MyoKardia
MyoKardia Announces Danicamtiv Data Presentation at the European Society of Cardiology’s Virtual Heart Failure Association Discoveries
June 18, 2020
Revolution Medicines
Revolution Medicines Appoints Eric T. Schmidt, Ph.D. and Peter Svennilson to its Board of Directors
June 17, 2020
Agios Pharmaceuticals
Agios to Present at the BMO 2020 Prescriptions for Success Healthcare Virtual Conference on Tuesday, June 23, 2020
June 17, 2020
Foundation Medicine
FoundationOne®CDx Receives FDA Approval as the First Companion Diagnostic to Identify Advanced Cancer Patients with Solid Tumors that are Tumor Mutational Burden-High (TMB-H) and Appropriate for Immunotherapy Treatment with KEYTRUDA® (pembrolizumab)
June 16, 2020
MyoKardia
MyoKardia to Present at Virtual BMO 2020 Prescriptions for Success Healthcare Conference
June 16, 2020
Nurix Therapeutics
Nurix Therapeutics Announces Addition Of Immuno-Oncology Clinical Experts To Its Management Team
June 15, 2020
Foundation Medicine
Foundation Medicine Appoints Dr. Geoffrey Oxnard as Vice President, Global Medical Lead, Liquid Franchise
June 15, 2020
Magenta Therapeutics
Magenta Therapeutics And Beam Therapeutics Announce Collaboration To Evaluate Targeted Antibody-Drug Conjugate (ADC) MGTA-117 As Conditioning Regimen For Base Editing Therapies
June 12, 2020
Agios Pharmaceuticals
Agios Announces Clinical Proof-of-Concept Has Been Established in Phase 1 Study of Mitapivat, First-in Class PKR Activator, in Sickle Cell Disease
June 12, 2020
Agios Pharmaceuticals
Agios First-in Class PKR Activator Mitapivat Demonstrates Sustained Hemoglobin Responses in Non-transfusion-dependent α- and β-Thalassemia in Phase 2 Study
June 12, 2020
bluebird bio
Majority of Evaluable Patients Across Genotypes Achieve Transfusion Independence and Maintain It with Near-Normal Hemoglobin Levels in Phase 3 Studies of betibeglogene autotemcel (LentiGlobin™ for β-thalassemia) Gene Therapy Presented at EHA Congress
June 12, 2020
bluebird bio
New Data Show Near Elimination of Sickle Cell Disease-Related Vaso-Occlusive Crises and Acute Chest Syndrome in Phase 1/2 Clinical Study of bluebird bio’s LentiGlobin™ Gene Therapy for Sickle Cell Disease at 25th EHA Congress
June 12, 2020
Constellation Pharmaceuticals
Constellation Pharmaceuticals Provides Updates of MANIFEST Study for CPI-0610 and EZH2 Franchise
June 12, 2020
Agios Pharmaceuticals
Agios and Royalty Pharma Announce $255 Million Purchase Agreement for IDHIFA® Royalty