July 29, 2020

Thrive Earlier Detection

Thrive Earlier Detection Closes $257 Million Series B Financing

July 29, 2020

Editas Medicine

Catalent Enters Into Strategic Partnership With Editas Medicine To Support Gene Editing Medicine Pipeline

July 29, 2020

bluebird bio

Bristol Myers Squibb and bluebird bio Announce Submission of Biologics License Application (BLA) to FDA for Idecabtagene Vicleucel (Ide-cel, bb2121) for Adults with Relapsed and Refractory Multiple Myeloma

July 27, 2020

Rhythm Pharmaceuticals

Rhythm Pharmaceuticals Announces Appointment of Joseph Shulman as Senior Vice President of Technical Operations

July 27, 2020

Editas Medicine

Editas Medicine Appoints Gad Berdugo As Chief Business Officer

July 27, 2020

Allena Pharmaceuticals

Allena Pharmaceuticals Announces $5.0 Million Bought Deal Offering

July 27, 2020

Allena Pharmaceuticals

Allena Pharmaceuticals Increases Previously Announced Bought Deal to $6.7 Million

July 24, 2020

Blueprint Medicines

Blueprint Medicines Receives Positive CHMP Opinion for Avapritinib for the Treatment of Adults with Unresectable or Metastatic PDGFRA D842V Mutant Gastrointestinal Stromal Tumors

July 23, 2020

Blueprint Medicines

Blueprint Medicines to Report Second Quarter 2020 Financial Results on Thursday, July 30, 2020

July 23, 2020

Editas Medicine

Editas Medicine To Host Conference Call Discussing Second Quarter 2020 Results And Corporate Update

July 23, 2020

MyoKardia

MyoKardia Announces Receipt of Breakthrough Therapy Designation from FDA for Mavacamten for the Treatment of Symptomatic, Obstructive Hypertrophic Cardiomyopathy

July 23, 2020

Nurix Therapeutics

Nurix Therapeutics Announces Pricing of $209 Million Initial Public Offering

July 21, 2020

MyoKardia

MyoKardia and Fulcrum Therapeutics Announce Multi-Target Collaboration to Discover Novel Targeted Therapies for Genetic Cardiomyopathies

July 21, 2020

Sage Therapeutics

Sage Therapeutics to Report Second Quarter 2020 Financial Results on Monday, August 10, 2020

July 20, 2020

Relay Therapeutics

Relay Therapeutics Announces Closing of Initial Public Offering and Full Exercise of Underwriters’ Option to Purchase Additional Shares

July 20, 2020

Rhythm Pharmaceuticals

Rhythm Pharmaceuticals Announces Appointment of David Meeker, M.D., as Chief Executive Officer

July 16, 2020

Agios Pharmaceuticals

Agios to Webcast Conference Call of Second Quarter 2020 Financial Results on July 30, 2020

July 16, 2020

Rhythm Pharmaceuticals

Rhythm Pharmaceuticals Announces Publication of Results from Phase 2 Study of Setmelanotide in Bardet-Biedl Syndrome in Diabetes, Obesity and Metabolismr

July 15, 2020

Relay Therapeutics

Relay Therapeutics Announces Pricing of Initial Public Offering

July 14, 2020

Blueprint Medicines

Blueprint Medicines Announces Global Collaboration with Roche to Develop and Commercialize Pralsetinib for Patients with RET-Altered Cancers

July 13, 2020

Nurix Therapeutics

Nurix Therapeutics Announces Addition of Dr. Jason Kantor to its Management Team

July 07, 2020

Editas Medicine

Editas Medicine And Azzur Group Announce A Multi-Year Agreement For EDIT-301 And EDIT-201 Manufacturing

July 06, 2020

MyoKardia

MyoKardia Announces Appointment of Denelle J. Waynick as General Counsel and Corporate Secretary

July 01, 2020

Rhythm Pharmaceuticals

Rhythm Pharmaceuticals Receives Rare Pediatric Disease Designation from U.S. Food and Drug Administration for Setmelanotide for Treatment of POMC and LEPR Deficiency Obesities

July 01, 2020

Rhythm Pharmaceuticals

Rhythm Pharmaceuticals Announces Submission of Marketing Authorization Application to the European Medicines Agency for Setmelanotide in POMC and LEPR Deficiency Obesities

July 01, 2020

Celsius Therapeutics

Celsius Therapeutics Signs Research Agreements with Leading Academic Centers to Develop Insights into Inflammatory Bowel Disease Biology

July 01, 2020

Blueprint Medicines

Blueprint Medicines Announces Submission of New Drug Application to FDA for Pralsetinib for the Treatment of Advanced RET Mutant and RET Fusion-Positive Thyroid Cancers

June 30, 2020

Revolution Medicines

Revolution Medicines Reports New Application of Tri-Complex Modality for “Undruggable” Protein Targets and Announces License to Ginkgo Bioworks to Explore Potential Use Against Novel Coronavirus

June 30, 2020

Goldfinch Bio

Goldfinch Bio Secures $100 Million in Series B Financing

June 29, 2020

Blueprint Medicines

Blueprint Medicines Announces Publication in The Lancet Oncology Showing Durable Clinical Benefits of AYVAKIT™ (avapritinib) in NAVIGATOR Trial Patients with PDGFRA D842V Mutant GIST

June 25, 2020

Nurix Therapeutics

Nurix Therapeutics Announces Formation Of DeCART Therapeutics To Advance New CAR T Therapies Using Targeted Protein Modulation

June 25, 2020

GBT

GBT Awards $250,000 in ACCEL Grants to Advance Access to Care for People Living with Sickle Cell Disease

June 24, 2020

GBT

GBT Announces Plans to Seek Regulatory Approval for Oxbryta® (voxelotor) to Treat Sickle Cell Patients in Europe

June 24, 2020

Fulcrum Therapeutics

Fulcrum Therapeutics Announces Initiation of Multi-Center Phase 3 (LOSVID) Trial with Losmapimod for Hospitalized COVID-19 Patients

June 22, 2020

CytomX Therapeutics

CytomX Therapeutics Announces Preclinical Data from Anti-CTLA-4 Probody Therapeutic Programs Presented by Partner Bristol Myers Squibb at AACR Annual Meeting

June 22, 2020

Jounce Therapeutics

Jounce Therapeutics Presents First Preclinical Data on Anti-CCR8 Antibody JTX-1811 and Vopratelimab Translational Data at The American Association for Cancer Research Virtual Annual Meeting

June 19, 2020

MyoKardia

MyoKardia Announces Danicamtiv Data Presentation at the European Society of Cardiology’s Virtual Heart Failure Association Discoveries

June 18, 2020

Revolution Medicines

Revolution Medicines Appoints Eric T. Schmidt, Ph.D. and Peter Svennilson to its Board of Directors

June 17, 2020

Agios Pharmaceuticals

Agios to Present at the BMO 2020 Prescriptions for Success Healthcare Virtual Conference on Tuesday, June 23, 2020

June 17, 2020

Foundation Medicine

FoundationOne®CDx Receives FDA Approval as the First Companion Diagnostic to Identify Advanced Cancer Patients with Solid Tumors that are Tumor Mutational Burden-High (TMB-H) and Appropriate for Immunotherapy Treatment with KEYTRUDA® (pembrolizumab)

June 16, 2020

MyoKardia

MyoKardia to Present at Virtual BMO 2020 Prescriptions for Success Healthcare Conference

June 16, 2020

Nurix Therapeutics

Nurix Therapeutics Announces Addition Of Immuno-Oncology Clinical Experts To Its Management Team

June 15, 2020

Foundation Medicine

Foundation Medicine Appoints Dr. Geoffrey Oxnard as Vice President, Global Medical Lead, Liquid Franchise

June 15, 2020

Magenta Therapeutics

Magenta Therapeutics And Beam Therapeutics Announce Collaboration To Evaluate Targeted Antibody-Drug Conjugate (ADC) MGTA-117 As Conditioning Regimen For Base Editing Therapies

June 12, 2020

Agios Pharmaceuticals

Agios Announces Clinical Proof-of-Concept Has Been Established in Phase 1 Study of Mitapivat, First-in Class PKR Activator, in Sickle Cell Disease

June 12, 2020

Agios Pharmaceuticals

Agios First-in Class PKR Activator Mitapivat Demonstrates Sustained Hemoglobin Responses in Non-transfusion-dependent α- and β-Thalassemia in Phase 2 Study

June 12, 2020

bluebird bio

Majority of Evaluable Patients Across Genotypes Achieve Transfusion Independence and Maintain It with Near-Normal Hemoglobin Levels in Phase 3 Studies of betibeglogene autotemcel (LentiGlobin™ for β-thalassemia) Gene Therapy Presented at EHA Congress

June 12, 2020

bluebird bio

New Data Show Near Elimination of Sickle Cell Disease-Related Vaso-Occlusive Crises and Acute Chest Syndrome in Phase 1/2 Clinical Study of bluebird bio’s LentiGlobin™ Gene Therapy for Sickle Cell Disease at 25th EHA Congress

June 12, 2020

Constellation Pharmaceuticals

Constellation Pharmaceuticals Provides Updates of MANIFEST Study for CPI-0610 and EZH2 Franchise

June 12, 2020

Agios Pharmaceuticals

Agios and Royalty Pharma Announce $255 Million Purchase Agreement for IDHIFA® Royalty

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